Tomorrow night, Max Randell will graduate from middle school. He even passed a test on the U.S. Constitution. I donít think I could do that.
Max has Canavan disease. And thanks to gene therapy, heís here to celebrate.
Canavan disease is an inherited disease that strips the insulation from nerve cells in the brain. It destroys neural function, beginning at birth and likely before, and the child loses the battle by age 8 -- unless she or he has gene therapy, still experimental (as are all gene therapies). (more…)